MLD UK registry news
Following long discussions around the current worldwide status of Registries for MLD and because of…
MLD adminJuly 12, 2021
Treating early onset MLD
We are pleased to report Orchard Therapeutics has received EC full (standard) market approval for…
MLD adminDecember 21, 2020
The Survey to understand the MLD patient and care-giver experience is now live
This research is extremely important for us to gather, so we can ensure that regulatory…
MLD adminAugust 28, 2020
Making a leap for rare diseases
Metachromatic Leukodystrophy (MLD) is classified as a Rare Disease There are over 300 million people…
MLD adminFebruary 27, 2020
A Study of Intrathecal SHP611 in Participants with Late Infantile MLD
A new Clinical Trial has been announced by Shire (now part of Takeda Pharmaceutical Company…
MLD adminDecember 14, 2018
Family Conference
The second MLD Support Association UK Family Conference was held at Wyboston Lakes in St.…
MLD adminJune 12, 2018
Scientific Conference
On Friday 8 June 2018, we held our second Scientific Conference at Wyboston Lakes in…
MLD adminJune 11, 2018